Use of adenine base editing and homology-independent targeted integration strategies to correct the cystic fibrosis causing variant, W1282X
- Mention, K.
- Cavusoglu-Doran, K.
- Joynt, A.T.
- Santos, L.
- Sanz, D.
- Eastman, A.C.
- Merlo, C.
- Langfelder-Schwind, E.
- Scallan, M.F.
- Farinha, C.M.
- Cutting, G.R.
- Sharma, N.
- Harrison, P.T.
ISSN: 1460-2083
Any de publicació: 2023
Volum: 32
Número: 23
Pàgines: 3237-3248
Tipus: Article